Developing Drugs for Rare Diseases: Pointers and Pitfalls

There are approximately 30 million individuals in the U.S. currently living with one of at least 7,000 rare diseases. The National Organization for Rare Disorders estimates that more than 90% of these patients are still without an FDA-approved treatment. Dr. Jane Larkindale, VP of Clinical Science at PepGen, Inc. is looking to change that, and she has both the experience and passion to show you how.